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Trisomy 13, also known as Patau syndrome, is a severe chromosomal disorder caused by the presence of an extra copy of chromosome 13. It leads to multiple congenital anomalies, particularly affecting the central nervous system, face, heart, and limbs, and is associated with high neonatal mortality.

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https://www.youtube.com/watch?v=QBussteAbA0

Genetics


Feature Description
Karyotype 47,XX,+13 or 47,XY,+13 in full trisomy
Mechanisms Full trisomy 13 (~75%)
Mosaicism (~5%) – milder phenotype
Unbalanced translocation (~20%) – may recur in families
Recurrence risk Low for full trisomy; higher for translocation carriers

Epidemiology


Feature Description
Incidence ~1 in 10,000–16,000 live births
Sex Equal male-to-female ratio
Risk factor Advanced maternal age increases risk

Clinical Features


Domain Features
Craniofacial Microphthalmia or anophthalmia
Cleft lip and/or palate
Microcephaly
Scalp defects (aplasia cutis)
Low-set malformed ears
• ‣
CNS • ‣ (classic finding)
Seizures
Severe intellectual disability
Hypotonia
CVS Congenital heart defects in >80%
• Ventricular septal defect (VSD)
• Atrial septal defect (ASD)
• Patent ductus arteriosus (PDA)
• Dextrocardia
Limb Anomalies Postaxial polydactyly (extra digit on ulnar side)
• ‣
• Overlapping fingers
Clenched hands
Genitourinary Cryptorchidism
Hydronephrosis
• Polycystic kidneys
• Uterine anomalies
Growth • ‣
• Poor postnatal weight gain

4. Prenatal Diagnosis

Modality Findings
Ultrasound • Holoprosencephaly (alobar/semi-lobar)
• Facial clefts
• Polydactyly
• IUGR
• Cardiac anomalies
• Omphalocele
• Single umbilical artery
Noninvasive screening (NIPT) Can detect trisomy 13 from maternal blood
Confirmatory tests Chorionic villus sampling (CVS) or amniocentesis with karyotyping or FISH

Radiology


Modality Imaging features
Brain (CT/MR) Holoprosencephaly: Failure of prosencephalon to divide; alobar is most severe
Ventriculomegaly: Often present
Midline facial defects: Cleft lip/palate, hypotelorism
Echo Structural cardiac anomalies (VSD, ASD, PDA)
Skeletal (XR) Polydactyly, overlapping digits, short long bones

Differentials


Condition Distinguishing Features
Trisomy 18 (Edwards syndrome) Prominent occiput, clenched fists, no polydactyly
Smith–Lemli–Opitz syndrome Cholesterol synthesis defect, 2nd–3rd toe syndactyly
Occipital encephalocele, cystic kidneys, polydactyly (but autosomal recessive)